Do More for ML4!
$107,947 raised
1079% of $10k goal
736 contributors
2 Years running

The ML4 Foundation’s mission is to fund, support, and promote medical research dedicated to developing treatments for Mucolipidosis Type IV (ML4), a genetic neurodegenerative storage disease.

Your donations directly support treatment-focused research at Massachusetts General Hospital, The Weizmann Institute, and other top laboratories around the world working on creating drugs to control neuro-inflammation and to create gene therapy for children with ML4.  You have a direct impact when you donate to ML4!

Your generous donations fund incredible research creating treatments for children with ML4. With dramatic cuts to NIH funding in recent years, researchers turn ever more to private foundations such as the ML4 Foundation for funding to keep their labs working on this disease. You can read more about the scientific research you are funding at We are particularly excited about a FDA-approved drug we are testing to control neuro-inflammation and restore function of neurons in the brain, and also about development of a gene therapy for ML4 that has already produced exciting data! Your donation helps this work succeed!


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